1. |
Acute Leukemia |
2. |
Adrenal Cancer - with distant metastases or inoperable, unresectable or recurrent |
3. |
Alexander Disease (ALX) - Neonatal and Infantile |
4. |
Amyotrophic Lateral Sclerosis (ALS) |
5. |
Anaplastic Adrenal Cancer - with distant metastases or inoperable, unresectable or recurrent |
6. |
Astrocytoma - Grade III and IV |
7. |
Bladder Cancer - with distant metastases or inoperable or unresectable |
8. |
Bone Cancer - with distant metastases or inoperable or unresectable |
9. |
Breast Cancer - with distant metastases or inoperable or unresectable |
10. |
Canavan Disease (CD) |
11. |
Cerebro Oculo Facio Skeletal (COFS) Syndrome |
12. |
Chronic Myelogenous Leukemia (CML) - Blast Phase |
13. |
Creutzfeldt-Jakob Disease (CJD) - Adult |
14. |
Ependymoblastoma (Child Brain Tumor) |
15. |
Esophageal Cancer |
16. |
Farber's Disease (FD) - Infantile |
17. |
Friedreichs Ataxia (FRDA) |
18. |
Frontotemporal Dementia (FTD), Picks Disease -Type A - Adult |
19. |
Gallbladder Cancer |
20. |
Gaucher Disease (GD) - Type 2 |
21. |
Glioblastoma Multiforme (Brain Tumor) |
22. |
Head and Neck Cancers - with distant metastasis or inoperable or uresectable |
23. |
Infantile Neuroaxonal Dystrophy (INAD) |
24. |
Inflammatory Breast Cancer (IBC) |
25. |
Kidney Cancer - inoperable or unresectable |
26. |
Krabbe Disease (KD) - Infantile |
27. |
Large Intestine Cancer - with distant metastasis or inoperable, unresectable or recurrent |
28. |
Lesch-Nyhan Syndrome (LNS) |
29. |
Liver Cancer |
30. |
Mantle Cell Lymphoma (MCL) |
31. |
Metachromatic Leukodystrophy (MLD) - Late Infantile |
32. |
Niemann-Pick Disease (NPD) - Type A |
33. |
Non-Small Cell Lung Cancer - with metastases to or beyond the hilar nodes or inoperable, unresectable or recurrent |
34. |
Ornithine Transcarbamylase (OTC) Deficiency |
35. |
Osteogenesis Imperfecta (OI) - Type II |
36. |
Ovarian Cancer - with distant metastases or inoperable or unresectable |
37. |
Pancreatic Cancer |
38. |
Peritoneal Mesothelioma |
39. |
Pleural Mesothelioma |
40. |
Pompe Disease - Infantile |
41. |
Rett (RTT) Syndrome |
42. |
Salivary Tumors |
43. |
Sandhoff Disease |
44. |
Small Cell Cancer (of the Large Intestine, Ovary, Prostate, or Uterus) |
45. |
Small Cell Lung Cancer |
46. |
Small Intestine Cancer - with distant metastases or inoperable, unresectable or recurrent |
47. |
Spinal Muscular Atrophy (SMA) - Types 0 And 1 |
48. |
Stomach Cancer - with distant metastases or inoperable, unresectable or recurrent |
49. |
Thyroid Cancer |
50. |
Ureter Cancer - with distant metastases or inoperable, unresectable or recurrent |